Fanconi Anemia
Bilde generert av AI
Stanford antibody regimen enables stem cell transplants without radiation or busulfan in Fanconi anemia
Rapportert av AI Bilde generert av AI Faktasjekket
A Stanford Medicine team reports that a single dose of the anti‑CD117 antibody briquilimab allowed three children with Fanconi anemia to undergo stem cell transplants without radiation or busulfan, achieving near‑complete donor cell engraftment in a phase 1b study published in Nature Medicine.