Intellia rapporterar starka fas iii-resultat för hae-behandling

Intellia Therapeutics presenterade huvudresultat från sin fas III-studie HALO gällande HAE under Bank of America Global Healthcare Conference den 12 maj. Resultaten visade på betydande kliniska fördelar för patienter med tillståndet.

Finansdirektör Edward Dulac beskrev resultaten som mycket uppmuntrande under sessionen. Alla patienter uppnådde en meningsfull klinisk nytta, där 62 procent förblev anfallsfria och terapifria vid slutet av den 28 veckor långa primära observationsperioden. Minskningen av anfallsfrekvensen nådde det höga 80-procentsintervallet, resultat som enligt Dulac matchar eller överträffar tidigare rapporter inom området.

Relaterade artiklar

Illustration of hemodialysis patient with fish oil supplements and PISCES trial graph showing 43% reduction in cardiovascular events.
Bild genererad av AI

High-dose fish oil linked to 43% fewer serious cardiovascular events in hemodialysis patients, trial reports

Rapporterad av AI Bild genererad av AI Faktagranskad

A large international randomized trial found that 4 grams a day of omega-3 fish oil was associated with a 43% lower rate of serious cardiovascular events among adults receiving maintenance hemodialysis. The PISCES study enrolled 1,228 participants at 26 sites in Australia and Canada; results were presented at the American Society of Nephrology’s Kidney Week 2025 and published in The New England Journal of Medicine.

HLS Therapeutics Inc. (TSX: HLS:CA) has published a slide deck for its 2025 fourth-quarter earnings call, released on March 13, 2026, following an earnings summary dated March 12, 2026.

Rapporterad av AI

Syntara Limited held a shareholder webinar on April 29 to discuss FDA feedback on its proposed Phase IIb trial for amsulostat in myelofibrosis, along with a capital raise and quarterly report. CEO Gary Phillips highlighted the agreed path forward with regulators. The company lodged its Appendix 4C quarterly with the ASX.

A repurposed breast cancer drug called MDL-001 has shown promise in lab and animal studies against a range of viruses, including flu, covid-19, RSV and norovirus. Developed by California-based Model Medicines using AI, the pill targets a conserved enzyme domain in viruses. A clinical trial is planned for early next year.

Rapporterad av AI

An experimental therapy using stem cells from young donors has shown promise in improving mobility for frail older people. In a trial involving 148 participants, infusions of laromestrocel led to significant gains in walking distance. Researchers highlight its potential to address biological roots of frailty.

A single injection of gene therapy has significantly improved hearing in all ten patients born with a genetic form of deafness, according to a new study. Researchers delivered a working copy of the OTOF gene into the inner ear, with most patients regaining hearing within one month. The treatment, tested in China, proved safe and effective across ages from one to 24.

Denna webbplats använder cookies

Vi använder cookies för analys för att förbättra vår webbplats. Läs vår integritetspolicy för mer information.
Avböj