Intellia rapporterar starka fas iii-resultat för hae-behandling

Intellia Therapeutics presenterade huvudresultat från sin fas III-studie HALO gällande HAE under Bank of America Global Healthcare Conference den 12 maj. Resultaten visade på betydande kliniska fördelar för patienter med tillståndet.

Finansdirektör Edward Dulac beskrev resultaten som mycket uppmuntrande under sessionen. Alla patienter uppnådde en meningsfull klinisk nytta, där 62 procent förblev anfallsfria och terapifria vid slutet av den 28 veckor långa primära observationsperioden. Minskningen av anfallsfrekvensen nådde det höga 80-procentsintervallet, resultat som enligt Dulac matchar eller överträffar tidigare rapporter inom området.

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